We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...
Myotonic muscular dystrophy is a common multi-system disorder that affects the skeletal muscles (the muscles that move ... An EKG to look at the heart rhythm, and frequently an echocardiogram to look ...
The musculoskeletal system is vital for physical health and includes three key components: muscular strength, endurance, and flexibility. If these areas are not maintained, you may experience weakened ...
in patients aged 2 to less than 18 years with spinal muscular atrophy (SMA) type 2. The randomized, double-blind, sham-controlled phase 3 STEER study (ClinicalTrials.gov Identifier: NCT05089656 ...
A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare ... therapies that stimulate muscle stem cell function have the potential to improve quality of life for DMD ...
Spinal muscular atrophy (SMA) is a rare genetic condition characterized by progressive muscle weakness and atrophy. It mainly affects motor function, but often also causes problems with speaking, ...