Sep. 25, 2024 — Adults with hemophilia B saw their number of bleeding episodes drop by an average of 71 percent after a single infusion of gene therapy, according to the new results of an ...
By Gina Kolata Photographs by Kenny Holston Gina Kolata visited Kendric Cromer and his parents for the third time as she has followed his gene therapy at Children’s National Hospital in ...
Sangamo's phase 1/2 STARR study data using isaralgagene civaparvovec targeting patients with Fabry Disease is expected in H1 2025. Learn more on SGMO stock here.