致力于开发创新疗法的临床阶段制药公司 Ractigen Therapeutics 宣布，美国食品药品监督管理局 (FDA) 已授予其针对 FUS 基因的新型 siRNA 疗法 RAG-21 孤儿药资格 (ODD) ，用于治疗肌萎缩侧索硬化症 (ALS ...

Quantum computing and biotech companies are testing whether next-generation computing technology could help them develop ...

RNA in cells performs an astounding number of functions. Messenger RNA carries the sequences of active genes to the cellular machinery, which turns... | Cell And Molecular Biology ...

Department of Biochemistry & Molecular Biophysics, Washington University School of Medicine, St. Louis, USA ...

In everyday life, when things turn out the opposite of what you expect, it's usually a cause for frustration. In science, ...

Optimizing Lead Discovery, Structural Analysis & Preclinical Modeling to Successfully Develop Stable, Effective & Orally Bioavailable Small Molecule RNA Drugs for Robust Translation into the ...

These signals are part of the intricate coordination of immune responses against virus invasion. With RNA increasingly seen as both a drug and a druggable target, the new findings open the potential ...

RNA-targeting compounds or small interfering RNAs (siRNAs) offer a potent means for controlling viral infections. An essential prerequisite to their design depends on identifying conserved and ...

New genetic drug delivery platform evades the liver allowing injected genetic material to reach target organs.

Filed provisional patent application, further expanding IP portfolio ...

研究成果以“诱导多能干细胞衍生的人静脉内皮细胞用于血管畸形建模和药物发现（Generation of iPSC-derived human venous endothelial cells for the modeling of vascular ...